https://www.whatisgenetherapy.com/ 2023-05-17 daily 1.0 https://www.whatisgenetherapy.com/Content/images/0.0_Parents_learn_about_childhood_genetic_desease_DT@2x.png Parent holds toddler close to their chest in loving embrace as child's hair blows in the wind https://www.whatisgenetherapy.com/Content/images/DNA_part_of_genes.png Illustration of the double helix of DNA https://www.whatisgenetherapy.com/Content/images/homepage-new-hope-arrow.svg https://www.whatisgenetherapy.com/Content/images/homepage-new-hope-arrow_hover.svg https://www.whatisgenetherapy.com/what-is-gene-therapy 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/what-is-gene-therapy-hero-graphic-mobile.png Young boy in electric wheel chair featuring a headrest looks off camera with alert expression https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-2.png https://www.whatisgenetherapy.com/Content/images/gene-replacement-video-thumbnail.png https://www.whatisgenetherapy.com/Content/images/gene-replacement-therapy-icon.png An illustration of a gene inside a vector to depict gene replacement therapy https://www.whatisgenetherapy.com/Content/images/gene-editing-or-crispr-cas9-icon.png An illustration of scissors to depict gene editoring or CRISPR Cas-9 https://www.whatisgenetherapy.com/Content/images/ex-vivo-gene-therapy-icon.png Illustration of petri dish and IV infusion bag depicting ex vivo gene therapy delivery https://www.whatisgenetherapy.com/Content/images/in-vivo-gene-therapy-icon.png IV infusion bag illustration depicting in vivo gene therapy delivery https://www.whatisgenetherapy.com/Content/images/adeno-associated-viral-vector-therapy-explained-graphic.png 3 steps of adeno-associated virus (AAV) therapy shown in illustration. 1) Functional gene is inserted into vector. 2) Vector travels to target location in the body. 3) Vector enters target cell and releases gene therapy. https://www.whatisgenetherapy.com/Content/images/2.2_how-delivered%20copy_M@4xKM.png 3 steps of adeno-associated virus (AAV) therapy shown in illustration. 1) Functional gene is inserted into vector. 2) Vector travels to target location in the body. 3) Vector enters target cell and releases gene therapy. https://www.whatisgenetherapy.com/Content/images/Arrow-down-green.png https://www.whatisgenetherapy.com/Content/images/Arrow-up-green.png https://www.whatisgenetherapy.com/Content/images/history-of-gene-therapy-1972-2022-table-graphic.png Gene therapy timeline. 50 years of advancements in treating genetic disease from 1972 to 2022. https://www.whatisgenetherapy.com/Content/images/history-of-gene-therapy-1972-2022-table-graphic-mobile.png Gene therapy timeline. 50 years of advancements in treating genetic disease from 1972 to 2022. https://www.whatisgenetherapy.com/Content/images/calendar-of-one-month-icon.png Calendar of one month icon https://www.whatisgenetherapy.com/Content/images/test-tube-containing-a-liquid-icon.png Test tube containing a liquid icon https://www.whatisgenetherapy.com/Content/images/pill-bottle-with-plus-sign-on-front-icon.png Pill bottle with plus sign on front https://www.whatisgenetherapy.com/Content/images/icon-of-hand-holding-a-test-tube-containing-liquid.png Icon of hand holding a test tube containing a liquid https://www.whatisgenetherapy.com/what-is-gene-therapy/ 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/what-is-gene-therapy-hero-graphic-mobile.png Young boy in electric wheel chair featuring a headrest looks off camera with alert expression https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-2.png https://www.whatisgenetherapy.com/Content/images/gene-replacement-video-thumbnail.png https://www.whatisgenetherapy.com/Content/images/gene-replacement-therapy-icon.png An illustration of a gene inside a vector to depict gene replacement therapy https://www.whatisgenetherapy.com/Content/images/gene-editing-or-crispr-cas9-icon.png An illustration of scissors to depict gene editoring or CRISPR Cas-9 https://www.whatisgenetherapy.com/Content/images/ex-vivo-gene-therapy-icon.png Illustration of petri dish and IV infusion bag depicting ex vivo gene therapy delivery https://www.whatisgenetherapy.com/Content/images/in-vivo-gene-therapy-icon.png IV infusion bag illustration depicting in vivo gene therapy delivery https://www.whatisgenetherapy.com/Content/images/adeno-associated-viral-vector-therapy-explained-graphic.png 3 steps of adeno-associated virus (AAV) therapy shown in illustration. 1) Functional gene is inserted into vector. 2) Vector travels to target location in the body. 3) Vector enters target cell and releases gene therapy. https://www.whatisgenetherapy.com/Content/images/2.2_how-delivered%20copy_M@4xKM.png 3 steps of adeno-associated virus (AAV) therapy shown in illustration. 1) Functional gene is inserted into vector. 2) Vector travels to target location in the body. 3) Vector enters target cell and releases gene therapy. https://www.whatisgenetherapy.com/Content/images/Arrow-down-green.png https://www.whatisgenetherapy.com/Content/images/Arrow-up-green.png https://www.whatisgenetherapy.com/Content/images/history-of-gene-therapy-1972-2022-table-graphic.png Gene therapy timeline. 50 years of advancements in treating genetic disease from 1972 to 2022. https://www.whatisgenetherapy.com/Content/images/history-of-gene-therapy-1972-2022-table-graphic-mobile.png Gene therapy timeline. 50 years of advancements in treating genetic disease from 1972 to 2022. https://www.whatisgenetherapy.com/Content/images/calendar-of-one-month-icon.png Calendar of one month icon https://www.whatisgenetherapy.com/Content/images/test-tube-containing-a-liquid-icon.png Test tube containing a liquid icon https://www.whatisgenetherapy.com/Content/images/pill-bottle-with-plus-sign-on-front-icon.png Pill bottle with plus sign on front https://www.whatisgenetherapy.com/Content/images/icon-of-hand-holding-a-test-tube-containing-liquid.png Icon of hand holding a test tube containing a liquid https://www.whatisgenetherapy.com/terms-of-use 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/how-genes-work 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/1.0_HERO_DT.png Enlarged illustration of the double helix of DNA https://www.whatisgenetherapy.com/Content/images/doublehelix-bg.png https://www.whatisgenetherapy.com/Content/images/transcription-turns-dna-into-rna-chart-graphic.png The double-stranded, double helix of DNA is transcribed into single-stranded RNA to be transcribed. RNA is translated into amino acids. It the precise order of these amino acids that leads the body to produce certain proteins. https://www.whatisgenetherapy.com/Content/images/demonstration-of-potential-variants-leading-to-a-genes-message-not-working-properly.png TCA changes to TAA. Then TCA is deleted. Next TCC is inserted between CAG and TCA. 3 new CAGs are inserted into in a series https://www.whatisgenetherapy.com/Content/images/demonstration-of-potential-variants-leading-to-a-genes-message-not-working-properly-mobile.png TCA changes to TAA. Then TCA is deleted. Next TCC is inserted between CAG and TCA. 3 new CAGs are inserted into in a series https://www.whatisgenetherapy.com/Content/images/single-gene-variant-as-cause-of-genetic-disease-icon.png Single gene variant as a cause of genetic disease is depicted as a dot on a chromosome icon https://www.whatisgenetherapy.com/Content/images/multiple-gene-variants-as-cause-of-genetic-disease-icon.png Multiple gene variants as a cause of genetic disease https://www.whatisgenetherapy.com/Content/images/chromosomal-variant-as-cause-of-genetic-diseases-icon.png Variations to chromosomes as a cause of genetic disease depicted as four dots in a circle icon https://www.whatisgenetherapy.com/privacy-policy 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/what-is-gene-therapy-used-for 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/what-is-gene-therapy-used-for-hero-graphic.png Teen-age girl in electronic wheelchair outside in park-like setting in summer looking at an attentive, friendly black and white dog. https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-3.png https://www.whatisgenetherapy.com/Content/images/blood-disorders-img.png https://www.whatisgenetherapy.com/Content/images/catheter.svg https://www.whatisgenetherapy.com/Content/images/3.0_2C_icon.png https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-newborn-icon.png Abstract illustration of newborn icon https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-adults-in-a-family-icon.png Abstract illustration of adults in a family icon https://www.whatisgenetherapy.com/Content/images/microscope-icon.png Microscope icon https://www.whatisgenetherapy.com/Content/images/00_arrow_inactive@2x.png https://www.whatisgenetherapy.com/Content/images/homepage-new-hope-arrow_hover.svg https://www.whatisgenetherapy.com/explore-more 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/Explore_more_about_gene_therapy_hero_graphic_DT.png Caring mother embraces son who lives with a genetic disease; both smiling wide and laughing as they share a joyful, loving moment. https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-3.png https://www.whatisgenetherapy.com/Content/images/Asset%209.png https://www.whatisgenetherapy.com/site-map 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/how-genes-work/ 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/1.0_HERO_DT.png Enlarged illustration of the double helix of DNA https://www.whatisgenetherapy.com/Content/images/doublehelix-bg.png https://www.whatisgenetherapy.com/Content/images/transcription-turns-dna-into-rna-chart-graphic.png The double-stranded, double helix of DNA is transcribed into single-stranded RNA to be transcribed. RNA is translated into amino acids. It the precise order of these amino acids that leads the body to produce certain proteins. https://www.whatisgenetherapy.com/Content/images/demonstration-of-potential-variants-leading-to-a-genes-message-not-working-properly.png TCA changes to TAA. Then TCA is deleted. Next TCC is inserted between CAG and TCA. 3 new CAGs are inserted into in a series https://www.whatisgenetherapy.com/Content/images/demonstration-of-potential-variants-leading-to-a-genes-message-not-working-properly-mobile.png TCA changes to TAA. Then TCA is deleted. Next TCC is inserted between CAG and TCA. 3 new CAGs are inserted into in a series https://www.whatisgenetherapy.com/Content/images/single-gene-variant-as-cause-of-genetic-disease-icon.png Single gene variant as a cause of genetic disease is depicted as a dot on a chromosome icon https://www.whatisgenetherapy.com/Content/images/multiple-gene-variants-as-cause-of-genetic-disease-icon.png Multiple gene variants as a cause of genetic disease https://www.whatisgenetherapy.com/Content/images/chromosomal-variant-as-cause-of-genetic-diseases-icon.png Variations to chromosomes as a cause of genetic disease depicted as four dots in a circle icon https://www.whatisgenetherapy.com/explore-more/ 2023-05-17 daily 0.9 https://www.whatisgenetherapy.com/Content/images/Explore_more_about_gene_therapy_hero_graphic_DT.png Caring mother embraces son who lives with a genetic disease; both smiling wide and laughing as they share a joyful, loving moment. https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-3.png https://www.whatisgenetherapy.com/Content/images/Asset%209.png https://www.whatisgenetherapy.com/what-is-gene-therapy-used-for/ 2023-05-17 daily 0.8 https://www.whatisgenetherapy.com/Content/images/what-is-gene-therapy-used-for-hero-graphic.png Teen-age girl in electronic wheelchair outside in park-like setting in summer looking at an attentive, friendly black and white dog. https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-3.png https://www.whatisgenetherapy.com/Content/images/blood-disorders-img.png https://www.whatisgenetherapy.com/Content/images/catheter.svg https://www.whatisgenetherapy.com/Content/images/3.0_2C_icon.png https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-newborn-icon.png Abstract illustration of newborn icon https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-adults-in-a-family-icon.png Abstract illustration of adults in a family icon https://www.whatisgenetherapy.com/Content/images/microscope-icon.png Microscope icon https://www.whatisgenetherapy.com/Content/images/00_arrow_inactive@2x.png https://www.whatisgenetherapy.com/Content/images/homepage-new-hope-arrow_hover.svg https://www.whatisgenetherapy.com/What-is-gene-therapy-used-for 2023-05-17 daily 0.8 https://www.whatisgenetherapy.com/Content/images/what-is-gene-therapy-used-for-hero-graphic.png Teen-age girl in electronic wheelchair outside in park-like setting in summer looking at an attentive, friendly black and white dog. https://www.whatisgenetherapy.com/Content/images/doublehelix-bg-3.png https://www.whatisgenetherapy.com/Content/images/blood-disorders-img.png https://www.whatisgenetherapy.com/Content/images/catheter.svg https://www.whatisgenetherapy.com/Content/images/3.0_2C_icon.png https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-newborn-icon.png Abstract illustration of newborn icon https://www.whatisgenetherapy.com/Content/images/abstract-illustration-of-adults-in-a-family-icon.png Abstract illustration of adults in a family icon https://www.whatisgenetherapy.com/Content/images/microscope-icon.png Microscope icon https://www.whatisgenetherapy.com/Content/images/00_arrow_inactive@2x.png https://www.whatisgenetherapy.com/Content/images/homepage-new-hope-arrow_hover.svg